A Study Evaluating the Safety and Pharmacokinetics of Aldurazyme® (Laronidase) in MPS I Patients Less Than 5 Years Old
Conditions
- Mucopolysaccharidosis I
- Hurler Syndrome
- Hurler-Scheie Syndrome
- Scheie Syndrome
Interventions
- BIOLOGICAL: Aldurazyme (Recombinant Human Alpha-L-Iduronidase)
- BIOLOGICAL: Aldurazyme (Recombinant Human Alpha-L-Iduronidase)
Sponsor
Genzyme, a Sanofi Company
Collaborators