Stem Cell Transplant for Inborn Errors of Metabolism

NCT00176904 · clinicaltrials.gov ↗

PHASE2,PHASE3

Phase

COMPLETED

Status

135

Enrollment

OTHER

Sponsor class

Conditions

Adrenoleukodystrophy
Metachromatic Leukodystrophy
Globoid Cell Leukodystrophy
Gaucher's Disease
Fucosidosis
Wolman Disease
Niemann-Pick Disease
Batten Disease
GM1 Gangliosidosis
Tay Sachs Disease
Sandhoff Disease

Interventions

PROCEDURE: Stem Cell Transplant
DRUG: Busulfan, Cyclophosphamide, Antithymocyte Globulin

Sponsor

Masonic Cancer Center, University of Minnesota