Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism

NCT00668564 · clinicaltrials.gov ↗

PHASE2

Phase

TERMINATED

Status

18

Enrollment

OTHER

Sponsor class

Stopped Replaced by another study

Conditions

Hurler's Syndrome
Maroteaux-Lamy Syndrome
Sly Syndrome
Alpha Mannosidosis
Fucosidosis
Aspartylglucosaminuria
Sphingolipidoses
Krabbe Disease
Wolman's Disease
Niemann-Pick Disease Type B
Niemann-Pick Disease, Type C

Interventions

PROCEDURE: Stem Cell Transplantation
DRUG: Cyclophosphamide
DRUG: Campath-1H
DRUG: Busulfan

Sponsor

Masonic Cancer Center, University of Minnesota