Kuvan® in Phenylketonuria Patients Less Than 4 Years Old
NCT01376908
·
clinicaltrials.gov ↗
PHASE3
Phase
COMPLETED
Status
56
Enrollment
INDUSTRY
Sponsor class
Conditions
Phenylketonuria
Interventions
DRUG:
Kuvan®
OTHER:
Phenylalanine (Phe)-restricted diet
Sponsor
BioMarin Pharmaceutical