Proteasomal Inhibition for Patients With Mis-sense Mutated Dysferlin
NCT01863004
·
clinicaltrials.gov ↗
PHASE1
Phase
TERMINATED
Status
3
Enrollment
OTHER
Sponsor class
Stopped
insufficient enrollment rate
Conditions
Dysferlinopathy
Interventions
DRUG:
Bortezomib
Sponsor
University Hospital, Basel, Switzerland