Sapropterin on Cognitive Abilities in Young Adults With Phenylketonuria
NCT01977820
·
clinicaltrials.gov ↗
PHASE2
Phase
TERMINATED
Status
2
Enrollment
INDUSTRY
Sponsor class
Stopped
Recruitment challenges
Conditions
Phenylketonuria
Interventions
DRUG:
Sapropterin
DRUG:
Placebo
Sponsor
BioMarin Pharmaceutical