Gene Therapy Study in Severe Haemophilia A Patients (270-201)
NCT02576795
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
15
Enrollment
INDUSTRY
Sponsor class
Conditions
Severe Haemophilia A
Interventions
BIOLOGICAL:
valoctocogene roxaparvovec
Sponsor
BioMarin Pharmaceutical