A Treatment Extension Study of Mucopolysaccharidosis Type IIIB
NCT03784287
·
clinicaltrials.gov ↗
PHASE2
Phase
UNKNOWN
Status
20
Enrollment
INDUSTRY
Sponsor class
Conditions
Mucopolysaccharidosis Type IIIB
MPS III B
Interventions
DRUG:
AX 250
Sponsor
Allievex Corporation