# Effect of Enzyme Replacement Therapy in Patients With Juvenile-onset Pompe Disease

> **NCT04942912** · — · UNKNOWN · sponsor: **Central Hospital, Nancy, France** · enrollment: 10 (estimated)

## Conditions studied

- Pompe's Disease Juvenile Onset

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT04942912
- **Lead sponsor:** Central Hospital, Nancy, France
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** UNKNOWN
- **Start date:** 2021-04-01
- **Primary completion:** 2021-06-30
- **Final completion:** 2021-07-30
- **Target enrollment:** 10 (ESTIMATED)
- **Last updated:** 2021-07-07


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT04942912

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT04942912, "Effect of Enzyme Replacement Therapy in Patients With Juvenile-onset Pompe Disease". Retrieved via MORVS 2026-10-13 from https://api.morvs.ai/clinical/NCT04942912. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*