Efficacy and Safety of Apitegromab in Patients With Later-Onset Spinal Muscular Atrophy Treated With Nusinersen or Risdiplam
Conditions
- Spinal Muscular Atrophy
- Spinal Muscular Atrophy Type 3
- Spinal Muscular Atrophy Type 2
- SMA
- Neuromuscular Diseases
- Muscular Atrophy
- Atrophy
- Muscular Atrophy, Spinal
- Neuromuscular Manifestations
- Anti-myostatin
Interventions
- DRUG: Apitegromab
- DRUG: Placebo
Sponsor
Scholar Rock, Inc.