A Gene Transfer Study Inducing Fetal Hemoglobin in Sickle Cell Disease (GRASP, BMT CTN 2001)

NCT05353647 · clinicaltrials.gov ↗

PHASE2

Phase

ACTIVE_NOT_RECRUITING

Status

25

Enrollment

OTHER

Sponsor class

Conditions

Sickle Cell Disease

Interventions

BIOLOGICAL: Autologous CD34+ HSC cells transduced with the lentiviral vector containing a shRNA targeting BCL11a

Sponsor

David Williams

Collaborators

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