Base-edited Autologous Hematopoietic Stem Cell Transplantation in Treating Patients With β-thalassemia Major

NCT06065189 · clinicaltrials.gov ↗
EARLY_PHASE1
Phase
COMPLETED
Status
2
Enrollment
OTHER
Sponsor class

Conditions

Interventions

Sponsor

Children's Hospital of Fudan University

Collaborators