Base-edited Autologous Hematopoietic Stem Cell Transplantation in Treating Patients With β-thalassemia Major
NCT06065189
·
clinicaltrials.gov ↗
EARLY_PHASE1
Phase
COMPLETED
Status
2
Enrollment
OTHER
Sponsor class
Conditions
Beta-Thalassemia
Interventions
BIOLOGICAL:
CS-101 injection
Sponsor
Children's Hospital of Fudan University
Collaborators
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