Global Study of Del-desiran for the Treatment of DM1
ACTIVE_NOT_RECRUITING
Status
Conditions
- DM1
- Myotonic Dystrophy
- Myotonic Dystrophy 1
- Myotonia
- Myotonic Dystrophy Type 1 (DM1)
- Dystrophy Myotonic
- Myotonic Disorders
- Steinert Disease
- Steinert
- Myotonic Muscular Dystrophy
Interventions
- DRUG: AOC 1001 (del-desiran)
- DRUG: Placebo
Sponsor
Avidity Biosciences, Inc.