A Repeat-Dose, Open-Label, Two Arm Safety and Efficacy Study of Two Doses of VP-001 Administered Intravitreally in Participants With Confirmed PRPF31 Mutation-Associated Retinal Dystrophy, Including Participants Previously Treated With VP001
Conditions
- Retinitis Pigmentosa 11
- Retinal Degeneration
- Retinal Disease
- Eye Diseases Hereditary
- Retinal Dystrophies
Interventions
Sponsor
PYC Therapeutics