A Clinical Trial of Elsunersen in Pediatric SCN2A-DEE to Assess Efficacy and Safety
Conditions
- Epileptic Encephalopathy
- SCN2A Encephalopathy
Interventions
- DRUG: 1mg elsunersen
- PROCEDURE: sham procedure
- DRUG: 0.5mg elsunersen
Sponsor
Praxis Precision Medicines