Managed Access Program for Del-zota in Participants With DMD Mutations Amenable to Exon 44 Skipping
Conditions
- Muscular Disorders, Atrophic
- Muscular Diseases
- Musculoskeletal Diseases
- Neuromuscular Diseases
- Nervous System Diseases
- Genetic Diseases, Inborn
- Genetic Diseases, X-Linked
- Muscular Dystrophies
- Muscular Dystrophy, Duchenne
Interventions
- DRUG: delpacibart zotadirsen
Sponsor
Avidity Biosciences, Inc.
Collaborators
- Clinigen Healthcare Limited