Tianasen (ASO-GNAO1) for GNAO1-Encephalopathy With Epilepsy and Movement Disorders.

NCT07363603 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

RECRUITING

Status

5

Enrollment

OTHER

Sponsor class

Conditions

GNAO1
Epilepsy
Hyperkinesis

Interventions

BIOLOGICAL: Antisense oligonucleotide treatment (ASO)

Sponsor

Pirogov Russian National Research Medical University