Expanded Access Protocol for Gene Therapy Utilizing shmiR Lentivirus Vector to Induce Fetal Hemoglobin in Sickle Cell Disease
NCT07640815
·
clinicaltrials.gov ↗
TEMPORARILY_NOT_AVAILABLE
Status
OTHER
Sponsor class
Conditions
Sickle Cell Disease
Interventions
BIOLOGICAL:
Autologous CD34+ HSC cells transduced with the lentiviral vector containing a shRNA targeting BCL11a
Sponsor
David Williams