A Phase I/II Trial of JR-446 in Mucopolysaccharidosis Type IIIB (MPS IIIB)
NCT07640984
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
RECRUITING
Status
12
Enrollment
INDUSTRY
Sponsor class
Conditions
Mucopolysaccharidosis IIIB
Interventions
DRUG:
JR-446
Sponsor
JCR Pharmaceuticals Co., Ltd.
Collaborators
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