AAVrh10-PCCA Gene Therapy for Propionic Acidemia

NCT07643844 · clinicaltrials.gov ↗

PHASE1

Phase

RECRUITING

Status

9

Enrollment

OTHER

Sponsor class

Conditions

Propionic Acidemia

Interventions

DRUG: AAVrh10-PCCA low dose
DRUG: AAVrh10-PCCA middle dose
DRUG: AAVrh10-PCCA high dose

Sponsor

Mayo Clinic