Safety and Efficacy of Avalglucosidase Alfa in Patients With Non-classic Pompe Disease Aged ≥ 5 Years

NCT07652814 · clinicaltrials.gov ↗

PHASE4

Phase

ACTIVE_NOT_RECRUITING

Status

6

Enrollment

OTHER

Sponsor class

Conditions

Glycogen Storage Disease Type II Late Onset
Pompe Disease (Late-onset)
Pompe Disease Late-Onset
Pompe's Disease Juvenile Onset
Pompe Disease

Interventions

DRUG: Avalglucosidase Alfa

Sponsor

Iris Plug

Collaborators

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