# Gene-Modified Stem Cell Therapy for Children With Autosomal Recessive Osteopetrosis (ARO)

> **NCT07665021** · PHASE1,PHASE2 · RECRUITING · sponsor: **Fondazione Telethon** · enrollment: 8 (estimated)

## Conditions studied

- Osteopetrosis

## Interventions

- **GENETIC:** FT024

## Key facts

- **NCT ID:** NCT07665021
- **Lead sponsor:** Fondazione Telethon
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** RECRUITING
- **Start date:** 2026-06-20
- **Primary completion:** 2030-06-20
- **Final completion:** 2031-06-30
- **Target enrollment:** 8 (ESTIMATED)
- **Last updated:** 2026-06-24

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT07665021

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT07665021, "Gene-Modified Stem Cell Therapy for Children With Autosomal Recessive Osteopetrosis (ARO)". Retrieved via MORVS 2026-10-21 from https://api.morvs.ai/clinical/NCT07665021. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*