Upadacitinib in Treatment of JAK/STAT Pathway Disorders With Activating Mutations
Conditions
- JAK1 GOF
- STAT1 GOF
- STAT3 GOF
- STAT5B GOF
- STAT6 GOF
Interventions
- DRUG: Upadacitinib
- DRUG: Placebo
Sponsor
Lisa Satter
Collaborators
- [object Object]
- [object Object]