Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials
Conditions
- Duchenne Muscular Dystrophy (DMD)
- Cardiomyopathy
- Becker Muscular Dystrophy
- Carrier of Duchenne Muscular Dystrophy
Sponsor
Vanderbilt University Medical Center
Collaborators