Study Evaluating a Gene Therapy for IPEX Syndrome Through the Expression of FOXP3 on Deficient T Cells to Produce Tregs-like.
Conditions
- The Immune Dysregulation Polyendocrinopathy Enteropathy X-linked Syndrome is a Primary Immunodeficiency Caused by Pathogenic Variants in Forkhead Box Protein 3
Interventions
- GENETIC: FOXP3-T4 drug product
- DRUG: ILT-101
Sponsor
Assistance Publique - Hôpitaux de Paris
Collaborators