Early Access Treatment With Tralesinidase Alfa in Mucopolysaccharidosis Type IIIB (Sanfilippo Syndrome Type B)
Conditions
- Mucopolysaccharidosis Type IIIB
- MPS IIIB (Sanfilippo B Syndrome)
Interventions
- DRUG: Tralesinidase alfa (TA)
Sponsor
Spruce Biosciences