Natural History Study: ENPP1 Deficiency or the Early-Onset Form of ABCC6 Deficiency
Conditions
- Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency
- ATP-Binding Cassette Subfamily C Member 6 Deficiency
- Generalized Arterial Calcification of Infancy
- Autosomal Recessive Hypophosphatemic Rickets
- PXE (Pseudoxanthoma Elasticum)
Sponsor
Inozyme Pharma