Preclinical Assessment of an Engineered HMGB1 Protein as a Novel Companion Therapy for Muscular Dystrophies
NCT07745218
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clinicaltrials.gov ↗
RECRUITING
Status
25
Enrollment
OTHER
Sponsor class
Conditions
LAMA2-MD (Merosin Deficient Congenital Muscular Dystrophy, MDC1A)
Sponsor
IRCCS San Raffaele